The world’s first personalized CRISPR therapy was delivered to an infant with urea cycle disorder (UCD) in just six months and was made possible with the contribution of coordinated expertise between Integrated DNA Technologies (IDT) and Aldevron.
IDT synthesized the CGMP guide RNA, led a comprehensive off-target safety analysis across over 300 genomic sites, and provided extensive regulatory support ensuring precision and safety at record speed.
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